Global Orphan Drug Market Size, Share, Growth, Trends, and Forecast (2024 - 2031)
Global Orphan Drug Market Scope: Historical Data (2021 – 2022), Base Year (2023), Forecast Period (2024 – 2031)
Market Segmentation: By Drug Type (Biological, and Non-Biological), Disease Type (Oncological diseases, Metabolic diseases, Hematologic & Immunologic diseases, Infectious diseases, Neurological diseases, and Other rare diseases), and Region (North America, Europe, Asia Pacific, Latin America, Middle East, and Africa)
Market Overview
The Global Orphan Drug Market was valued at USD 169,774.4 million in 2023 and is expected to reach USD 423,367.2 million by 2031 while growing at a CAGR of 12.1% during the forecast period (2024-2031).
*Note: Graph is shown for illustrative purposes only; complete datasets will be provided in the full report
Market Dynamics
This section of the report will analyze various driving and restraining factors that are expected to have a significant impact on the global orphan drug market growth. Certain drugs, known as orphan drugs, are designated a special status when they exhibit potential in treating, preventing, or diagnosing orphan diseases. An orphan disease refers to a rare condition impacting fewer than 200,000 individuals in the United States.
Regulatory incentives, a high unmet medical need, and growing awareness propel market growth. Conversely, small patient populations and high development costs impede market expansion.
Furthermore, the global orphan drug industry will be analyzed through various tools including PESTLE analysis, and Porter’s analysis.
Segmentation – By Drug Type Analysis
The Global Orphan Drug Market is segmented among Biological, and Non-Biological, based on Drug Type. In 2023, Biological accounted for the majority of the market share*.
*Note: Graph is shown for illustrative purposes only; complete datasets will be provided in the full report
Segmentation – By Disease Type Analysis
The Global Orphan Drug Market is segmented among Oncological diseases, Metabolic diseases, Hematologic & Immunologic diseases, Infectious diseases, Neurological diseases, and Other rare diseases, based on Disease Type. In 2023, Oncological diseases accounted for the majority of the market share*.
*Note: Graph is shown for illustrative purposes only; complete datasets will be provided in the full report
Global Orphan Drug Market: Regional Analysis
Based on region, the market is divided into six regions including North America, Europe, Asia Pacific, Latin America, Middle East, and Africa. In 2023, North America dominated the market with the highest market share, while Asia Pacific is expected to grow with the highest CAGR during the forecast period (2024 – 2031).
*Note: Graph is shown for illustrative purposes only; complete datasets will be provided in the full report
Competitive Landscape
Some of the key players operating in the market are Alexion Pharmaceuticals, Bristol-Myers Squibb Company (Celgene Corporation), Novartis AG, Pfizer Inc., F. Hoffmann-La Roche Ltd, Takeda Pharmaceutical Company Limited, Amgen Inc., Sanofi S.A, Johnson & Johnson, AstraZeneca Plc, and AbbVie Inc.
Table of Contents:
1. Research Methodology and Market Scope
Research Methodology
Market Scope
2. Executive Summary
3. Global Orphan Drug Market Dynamics
Drivers
Restraints
Opportunity
4. Global Orphan Drug Industry Analysis
PEST Analysis
Porter's Five Force Analysis
Recent Deals Analysis
5. Global Orphan Drug Market Segmentation, By Drug Type
Global Orphan Drug Market Share Analysis, By Drug Type
Global Orphan Drug Market Growth Analysis, By Drug Type
Global Orphan Drug Market Trends, By Drug Type
o Biological
o Non-Biological
6. Global Orphan Drug Market Segmentation, By Disease Type
Global Orphan Drug Market Share Analysis, By Disease Type
Global Orphan Drug Market Growth Analysis, By Disease Type
Global Orphan Drug Market Trends, By Disease Type
o Oncological diseases
o Metabolic diseases
o Hematologic & Immunologic diseases
o Infectious diseases
o Neurological diseases
o Other rare diseases
7. Global Orphan Drug Market Segmentation, By Region
Global Orphan Drug Market Share Analysis, By Region
Global Orphan Drug Market Growth Analysis, By Region
Global Orphan Drug Market Trends, By Region
o North America
o Europe
o Asia Pacific
o Latin America
o Middle East
o Africa
8. Competitive Landscape
Alexion Pharmaceuticals*
o Company Overview
o Financial Performance
o Key Development/Strategies
o SWOT Analysis
Bristol-Myers Squibb Company (Celgene Corporation)
Novartis AG
Pfizer Inc.
F. Hoffmann-La Roche Ltd
Takeda Pharmaceutical Company Limited
Amgen Inc.
Sanofi S.A
Johnson & Johnson
AstraZeneca Plc
AbbVie Inc
*Similar analysis will be provided for each company listed above.
